Alexander disease
Aug. 25, 2024
Amy T Waldman MD MSCE
Associate Professor of Neurology
Medical Director, Leukodystrophy Center of Excellence
Children's Hospital of Philadelphia
Perelman School of Medicine at the University of Pennsylvania
Contributor Disclosures
Dr. Waldman of Children's Hospital of Philadelphia Research Institute served as principal investigator in a clinical trial and received research support from Ionis Pharmaceuticals.